Agilis Partners with Japanese Research Institute to Develop Gene Therapy for Angelman, Other Rare Conditions
Agilis Biotherapeutics is collaborating with the Gene Therapy Research Institution (GTRI) in Japan to develop and manufacture a new adeno-associated virus (AAV) gene therapy for Angelman syndrome (AS) and other rare genetic disorders. Angelman patients lack the maternal copy of the UBE3A gene. In certain brain areas, only…