• European Initiative Targets Diagnosis, Treatment of Rare Diseases
  • Anxiety Common in Older Children and Especially Evident When ‘Preferred’ Caregiver Absent, Study Says
  • Ovid Starts Phase 3 Trial of Experimental Therapy for Kids with Angelman
  • World’s First Alport Stamp Is Macedonian Mom’s Latest Win for Rare Disease Patients
  • NORD Honors Industry, Patient Advocates at Rare Impact Awards Gala
  • 20-Year Mystery of Girl with Angelman and 2nd Rare Disease Solved via Genetic Testing
  • Eurordis Unveils Integrated-care Initiative for Rare Disease Patients
  • ‘Rare Barometer’ Program Helps Eurordis Shape EU Rare Disease Policy
  • Familiarity Is the Foundation for Acceptance
  • Scientists Develop Quick, Accurate Diagnostic Test for Angelman and Prader-Willi Syndromes
  • Agency Unveils RaDaR to Help Patient Groups Develop Rare Disease Registries
  • Roche Researcher Plans Clinical Trial Seeking Ways to Measure Disease Impact in Home and Clinic